Medical Director

Summary

Join Ultragenyx as a Medical Director and contribute to the development of gene therapies for rare diseases. You will provide strategic medical leadership, support the execution of medical launch plans, and develop integrated evidence generation plans. Responsibilities include collaborating with key opinion leaders, supporting payer activities, and partnering with cross-functional teams. The role requires an MD or DO with board certification in a relevant field and experience in managing patients with inherited metabolic disorders. A remote work model is offered with occasional travel. Competitive salary, bonus, equity incentives, and a range of benefits are included.

Requirements

• Medical Doctor (MD, DO) with Board certification (or equivalent) in Biochemical/Metabolic Genetics or Endocrinology (required)
• Experience in the management of patients with inherited metabolic disorders
• Comfortable with ambiguity and developing innovative approaches, ability to work independently and as a member of an integrated, interdisciplinary team
• Proven leadership skills including a passion for collaboration and understanding all stakeholder perspectives to drive alignment and decision-making
• Excellent speaking and writing skills, with a demonstrated ability to effectively communicate with a broad range of internal and external stakeholders, including medical professionals, and the general public
• Highly analytical and strategic thinker with the ability to identify interdependencies, consider the medical implications and understand the broader goals of a program and the organization
• High aptitude for attention to detail, demand for high-quality work, and sense of passion and urgency to achieve goals and improve the lives of patients

Responsibilities

• Provide strategic medical and scientific leadership to assigned program(s) to support development of the global medical strategy
• Support the execution of the medical launch plan for the relevant programs
• Support development of the integrated evidence generation plan for assigned program(s), including input to Disease Monitoring Programs and leading data generation activities
• Support the execution of the relevant medical affairs activities including advisory boards, medical education initiatives, congress activities, and payer interactions
• Provide medical expertise across the organization to compliantly assist in the development and execution of commercial and clinical development activities
• Participate in scientific engagement and maintain strong relationships with external stakeholders (including healthcare professionals, clinical investigators, and societies) to generate insights and to educate and advance scientific understanding of relevant disease area
• Provide scientific and medical leadership as needed for publication development and serve as medical affairs reviewer for promotional materials and non-promotional scientific materials
• Provide support for Medical Science Liaison activities. This will include training as well as development of materials
• Partner cross functionally within medical affairs on assigned programs with all key stakeholders e.g., regional medical teams, US field medical, training, health economics and outcomes research, molecular diagnostics, medical services, patient find, patient advocacy, commercial, regulatory, clinical development and other related departments
• Exhibit leadership skills within and outside of the organization (including collaboration, mentoring, presentation skills and professional interaction)

Preferred Qualifications

• At least 2 years of experience in the pharmaceutical industry is strongly preferred, with Medical Affairs experience being ideal; however, extensive relevant clinical experience may be considered as an alternative
• Clinical or industry experience in gene therapy is preferred

Benefits

• Generous vacation time and public holidays observed by the company
• Volunteer days
• Long term incentive and Employee stock purchase plans or equivalent offerings
• Employee wellbeing benefits
• Fitness reimbursement
• Tuition sponsoring
• Professional development plans
• Annual bonus
• Equity incentives
• Remote work